Publication
| Rha AK, Kan SH, Andrade-Heckman P, Christensen CL, Harb JF, Wang RY, Base editing of the GLB1 gene is therapeutic in GM1 gangliosidosis patient-derived cells Molecular genetics and metabolism143:108568 2024 |
| PubMed ID: 39303319 |
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| Records Return:
(1)
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| Catalog ID | Sex | Age at Sampling | Description | Collection_Type_id |
| GM03589 | Female | 7 MO | GANGLIOSIDOSIS, GENERALIZED GM1, TYPE I | GM |
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