Publication
| Bobo TA, Robinson M, Tofade C, Sokolski-Papkov M, Nichols P, Vorobiov S, Fu H, AAV gene replacement therapy for treating MPS IIIC: Facilitating bystander effects via EV-mRNA cargo Journal of extracellular vesicles13:e12464 2024 |
| PubMed ID: 38961538 |
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| Records Return:
(2)
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| Catalog ID | Sex | Age at Sampling | Description | Collection_Type_id |
| GM00969 | Female | 2 YR | APPARENTLY HEALTHY INDIVIDUAL | GM |
| GM05157 | Male | 8 YR | MUCOPOLYSACCHARIDOSIS TYPE IIIC | GM |
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