Publication
| Zhang J, Frabutt DA, Chrzanowski M, Li N, Miller LM, Tian J, Mulcrone PL, Lam AK, Draper BE, Jarrold MF, Herzog RW, Xiao W, A novel class of self-complementary AAV vectors with multiple advantages based on cceAAV lacking mutant ITR Molecular therapy Methods & clinical development32:101206 2024 |
| PubMed ID: 38390555 |
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| Records Return:
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| Catalog ID | Sex | Age at Sampling | Family | Relationship | Description | Collection_Type_id |
| GM16095 | Female | 3 YR | 1875 | proband | COCKAYNE SYNDROME, TYPE B; CSB | GM |
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